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- $6.7BMarket Cap
- 63.23%1-Year Change
- BiotechnologyIndustry
PTC Therapeutics (PTCT)
Key Performance
More- Earnings Score: 23
- Momentum Score: 85
- True Yield: N/A
- Financial Health Score: 71
Latest Research & News
What's Going On With Royalty Pharma Stock Wednesday?
Royalty Pharma acquired the final portion of PTC Therapeutics' royalty on Roche's Evrysdi for $240 million upfront plus up to $60 million in milestones, giving it 100% ownership of the 8-16% tiered royalty. Evrysdi generated $1.9 billion in 2024 sales with projected growth to $2.9 billion by 2030. RPRX stock is up 53% year-to-date but down slightly on Wednesday. The company also recently acquired royalty interests in Nuvalent's cancer drugs.
12/31/2025, 10:47 AM • Benzinga
Royalty Pharma has acquired the final portion of PTC Therapeutics' remaining royalty on Roche's Evrysdi for $240 million upfront plus up to $60 million in sales-based milestones. Following the transaction, Royalty Pharma will own 100% of the tiered 8% to 16% royalty on worldwide net sales of Evrysdi, an FDA-approved spinal muscular atrophy treatment that generated approximately $1.9 billion in sales in 2024 with projected growth to $2.9 billion by 2030.
12/29/2025, 4:40 PM • Benzinga
Here's Why Shares in PTC Therapeutics Soared This Week
PTC Therapeutics' CEO Matthew Klein highlighted the commercial potential of Sephience, a drug for treating phenylketonuria (PKU), projecting significant market opportunities in the U.S. and internationally. The company expects to reach cash flow breakeven with growing sales and believes most patients will respond positively to the treatment.
09/05/2025, 8:35 AM • The Motley Fool
Novartis reported strong Q2 2025 financial performance with 11% sales growth, double-digit core operating income increase, and raised full-year guidance. Key growth drivers included oncology and specialty medicine brands like Kisqali, Entresto, and Pluvicto.
07/17/2025, 1:00 AM • GlobeNewswire
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MoreInformation as of 06/22/2026
Company Profile
PTC Therapeutics, Inc., a biopharmaceutical company, focuses on the discovery, development, and commercialization of medicines to children and adults living with rare disorders in the United States and internationally. The company provides Translarna and Emflaza for the treatment of Duchenne muscular dystrophy; Upstaza to treat aromatic l-amino acid decarboxylas (AADC) deficiency, a central nervous system disorder; Tegsedi and Waylivra for the treatment of rare diseases; and Evrysdi to treat spinal muscular atrophy (SMA) in adults and children. Its development pipeline products include Sepiapterin for the treatment of phenylketonuria; PTC518 splicing platform, which is being developed for the treatment of Huntington's disease; and inflammation and ferroptosis platforms, including vatiquinone to treat Friedreich's ataxia. The company distributes its products through third-party distributors. It has collaborations with F. Hoffman-La Roche Ltd., Hoffman-La Roche Inc., the SMA Foundation, National Taiwan University, Akcea Therapeutics, Inc., and Shiratori Pharmaceutical Co., Ltd. The company has license and collaboration agreement with Novartis Pharmaceuticals Corporation to develop PTC518 Huntington's disease program. It markets Upstaza, a gene therapy with the brand name Kebilidi in the United States. PTC Therapeutics, Inc. was incorporated in 1998 and is headquartered in Warren, New Jersey.
Key Executives
- Matthew Klein
- Eric Pauwels
- Pierre Gravier
- Lee Golden
- Neil Almstead
Current Ownership Distribution
- Institutions1.5B (59.20%)
- Mutual Funds997.6M (40.60%)
- Insiders4.8M (0.20%)
- Other0 (0.00%)